Autism-related genes may shape early brain development via the extracellular matrix

A team of researchers from the University of Aberdeen has uncovered, for the first time, how genes linked to autism and ...
Technology Networks

When and Where Autism Genes Act in the Developing Brain

By analyzing over 213,000 developing human brain cells, researchers show that many autism risk genes act through the ECM.

Scientists identify first non-coding gene that controls cell size

What keeps our cells the right size? Scientists have long puzzled over this fundamental question, since cells that are too ...
NOLA.com

They said he couldn’t be a pilot with sickle cell. Gene therapy could change that.

This story is the first in an occasional series following Louisiana’s first patients to receive gene therapy for sickle cell disease. On the third floor of Manning Family Children’s Hospital in New ...
FiercePharma

For struggling cell and gene therapy field, Peter Marks' FDA exit adds even more uncertainty

The sudden resignation of Peter Marks, M.D., Ph.D., from the FDA branch that regulates biological products for humans laid bare the vaccine skepticism underpinning Robert F. Kennedy Jr.’s new ...
The New York Times

First Day of a ‘New Life’ for a Boy With Sickle Cell

Kendric Cromer, 12, is among the first patients to be treated with gene therapy just approved by the F.D.A. that many other patients face obstacles to receiving. By Gina Kolata Photographs by Kenny ...
FierceBiotech

CSL Behring shuts down California cell and gene therapy R&D site amid group pivot

In another sign of biopharma's waning interest in the traditional ex vivo gene therapy approach, CSL Behring is shutting down its U.S. R&D hub for cell and gene therapy in Pasadena, California, Fierce ...